BioMarin(美國(guó))
BioMarin Pharmaceutical
美國(guó)BioMarinPharmaceutical www.bmrn.com美國(guó)生物制藥公司BioMarinBioMarindevelopsandcommercializesinnovativebiopharmaceuticalsforseriousdiseasesandmedicalconditions,focusingonproductcandidatesthat:Addresscurrentl
yunmetmedicalneedsSuggestaclear-cutdevelopmentprofileProvideanopportunitytobefirst-to-marketThecompany'sproductportfolioiscomprisedofthreeapprovedproductsandmultipleinvestigationalproductcandidates.FDA-approvedproductsincludeKuvan®(sapropterindihydrochloride)TabletsforPKU,anoralsmallmoleculetherapeuticdevelopedinpartnershipwithMerckSerono;Naglazyme®(galsulfase)formucopolysaccharidosisVI(MPSVI),aproductwhollydevelopedandcommercializedbyBioMarin;andAldurazyme®(laronidase)formucopolysaccharidosisI(MPSI),aproductwhichBioMarindevelopedthrougha50/50jointventurewithGenzymeCorporation.Investigationalproductcandidatesi